(INNS)
AGURACINGEN KADOPARVOVEK(INNC)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 8 (RAAV8) VECTOR ENCODING CODON-OPTIMIZED HUMAN RETINAL CONE CYCLIC NUCLEOTIDE-GATED CATION CHANNEL ALPHA3 (CNGA3), UNDER CONTROL OF A SYNTHETIC PROMOTER, DERIVED FROM THE HUMAN OPSIN LOCUS CONTROL REGION AND THE HUMAN GREEN-SENSITIVE OPSIN GENE PROMOTER, TERMINATED WITH THE SIMIAN VIRUS 40 (SV40) POLYADENYLATION (POLYA) SEQUENCE, AND FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS)(WHO)
AGURACINGENUM CADOPARVOVECUM(INN)