(INNS)
ALNUGRANOGEN ALDEPARVOVEK(INNC)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 1 (AAV1) VECTOR ENCODING CODON-OPTIMISED HUMAN PROGRANULIN (PGRN, GRANULIN PRECURSOR), UNDER CONTROL OF A CYTOMEGALOVIRUS IMMEDIATE EARLY ENHANCER/CHICKEN BETA-ACTIN PROMOTER (THE CB7 PROMOTER) PLUS A CHIMERIC INTRON, CONSISTING OF A CHICKEN BETA-ACTIN SPLICE DONOR AND A RABBIT BETA-GLOBIN (RBG) SPLICE ACCEPTOR, TERMINATED WITH A RABBIT ALPHA-GLOBIN POLYADENYLATION SIGNAL, FLANKED BY ADENO-ASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS (ITRS).(WHO)
ALNUGRANOGENUM ALDEPARVOVECUM(INN)