(INNS)
ALVAMEMUGEN SULSEPARVOVEK(INNC)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS (RAAV) VECTOR WITH A LIVER-TROPHIC LK03 CAPSID, ENCODING CODON-OPTIMISED HUMAN METHYLMALONYL-COA MUTASE (MMUT, ALSO REFERRED TO AS MUT), PRECEDED BY THE SELF-CLEAVING 2A-PEPTIDE OF PORCINE TESCHOVIRUS 1, BORDERED BY HUMAN ALBUMIN (ALB) HOMOLOGY ARMS, AND ALL FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS).(WHO)
ALVAMEMUGENUM SULSEPARVOVECUM(INN)