(INNS)
BOMTABEGAGEN BAVOPARVOVEK(INNC)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR ENCODING HUMAN LYSOSOMAL ACID BETA-GALACTOSIDASE (GLB1), UNDER CONTROL OF A CYTOMEGALOVIRUS IMMEDIATE EARLY ENHANCER FUSED TO A CHICKEN BETA-ACTIN PROMOTER, A CHIMERIC INTRON CONTAINING SPLICE DONOR SITE OF THE CHICKEN BETA-ACTIN INTRON AND SPLICE ACCEPTOR SITE OF THE RABBIT BETA-GLOBIN GENE, AND TERMINATED WITH THE SIMIAN VIRUS 40 (SV40) POLYADENYLATION SEQUENCE, FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS)(WHO)
BOMTABEGAGENUM BAVOPARVOVECUM(INN)