(INNS)
BRINRETIGEN VESGEDPARVOVEC(INND)
BRINRETIGEN VESGEDPARVOVEK(INNC)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 5 (RAAV5) VECTOR ENCODING (1) CODONOPTIMIZED STAPHYLOCOCCUS AUREUS CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEATS (CRISPR)- ASSOCIATED PROTEIN 9 (CAS9) FLANKED BY SIMIAN VIRUS 40 (SV40) NUCLEAR LOCALISATION SIGNAL PEPTIDE SEQUENCES AND (2) TWO GUIDE RNAS (GRNA-323 AND GRNA-64) TARGETING INTRON 26 OF THE HUMAN CENTROSOMAL PROTEIN 290 (CEP290, NEPHROCYSTIN-6) GENE...PROPOSED INN: LIST 129, RECOMMENDED INN: LIST 91(WHO)
BRINRETIGENUM VESGEDPARVOVECUM(INN)