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CLEMIDSOGEN LANPARVOVEC
CLEMIDSOGÉN LANPARVOVEC
CLÉMIDSOGENE LANPARVOVEC
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR ENCODING HUMAN IDURONATE 2-SULFATASE (IDS, ALFA-L-IDURONATE SULFATE SULFATASE) UNDER CONTROL OF A HUMAN CYTOMEGALOVIRUS (CMV) IMMEDIATEEARLY ENHANCER/CHICKEN BETA-ACTIN (CBA) PROMOTER, WITH A CHICKEN BETA-ACTIN INTRON, TERMINATED WITH THE RABBIT BETA-GLOBIN POLYADENYLATION SIGNAL, AND FLANKED BY ADENOASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS (ITRS)