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ÉLIVALDOGENE AUTOTEMCEL
AUTOLOGOUS CD34+ HEMATOPOIETIC STEM CELLS TRANSDUCED EX VIVO WITH ELIVALDOGENE TAVALENTIVEC (115)(77), A VSV-G*-PSEUDOTYPED SELF-INACTIVATING HIV-1-DERIVED LENTIVIRAL VECTOR (PLBP100 HALD) ENCODING HUMAN ADRENOLEUKODYSTROPHY (ALD) PROTEIN (ABCD1 GENE) UNDER THE CONTROL OF A MODIFIED MYELOPROLIFERATIVE SARCOMA VIRUS PROMOTER (MND**) * VSV-G = VESICULAR STOMATITIS VIRUS G ENVELOPE PROTEIN ** MND = MYELOPROLIFERATIVE SARCOMA VIRUS ENHANCER WITH NEGATIVE CONTROL REGION DELETED, DL587REV PRIMERBINDING SITE SUBSTITUTED