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WHO 11369
LG7B4QT3EN
ENTACINGEN TURIPARVOVEC
A REPLICATION-DEFECTIVE ADENO-ASSOCIATED VIRAL VECTOR ENCODING CONE PHOTORECEPTOR CYCLIC NUCLEOTIDE-GATED CHANNEL BETA3 (CNGB3). A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRAL VECTOR SEROTYPE 8 (RAAV8), ENCODING CODON-OPTIMISED HUMAN CONE PHOTORECEPTOR CYCLIC NUCLEOTIDE GATED CHANNEL BETA3 (CNGB3), UNDER THE CONTROL OF THE HUMAN CONE ARRESTIN (HCAR) PROMOTER AND AN SV40 POLY(A) SEQUENCE, FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITR)