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GIROCTOCOGEN FITELPARVOVEC
RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/6 (RAAV REP2-CAP6) VECTOR, ENCODING HUMAN B-DOMAIN-DELETED BLOOD COAGULATION FACTOR VIII (HF8, FVIII) UNDER THE CONTROL OF A SYNTHETIC LIVER-SPECIFIC PROMOTER
RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/6 (RAAV6) VECTOR, ENCODING HUMAN B-DOMAIN-DELETED BLOOD COAGULATION FACTOR VIII (HF8, FVIII) UNDER THE CONTROL OF A SYNTHETIC LIVER-SPECIFIC PROMOTER; REC. INN LIST 84