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LENADOGEN NOLPARVOVEC
LENADOGÉNE NOLPARVOVEC
LÉNADOGENE NOLPARVOVEC
NON-REPLICATING SINGLE STRANDED DNA RECOMBINANT ADENO- ASSOCIATED VIRUS (RAAV) SEROTYPE 2 CONTAINING HUMAN WT MT-ND4 CDNA THAT ENCODES NADH DEHYDROGENASE SUBUNIT 4, UNDER THE CONTROL OF THE CYTOMEGALOVIRUS IMMEDIATE EARLY (CMVIE) PROMOTER IN AN INTRON-CONTAINING EXPRESSION CASSETTE (BETA GLOBIN INTRON, HBB2), FLANKED BY THE VIRAL INVERTED TERMINAL REPEATS FROM AAV2/2