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RANUZIFIGEN CIVAPARVOVEC
RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/6 (RAAV REP2-CAP6) VECTOR, EXPRESSING A CDNA THAT TARGETS 468- 485 BP OF THE ALBUMIN LOCUS (RELATIVE TO THE TRANSCRIPTION INITIATION SITE), FUSED TO THE OBLIGATE HETERODIMERIC FOKI NUCLEASE DOMAIN KKR, UNDER THE CONTROL OF AN APOLIPOPROTEIN E HEPATIC CONTROL REGION AND HUMAN ALPHA-1-ANTITRYPSIN PROMOTER (APOE/HAAT)
RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/6 (RAAV6) VECTOR, EXPRESSING A CDNA THAT TARGETS 468-485 BP OF THE ALBUMIN LOCUS (RELATIVE TO THE TRANSCRIPTION INITIATION SITE), FUSED TO THE OBLIGATE HETERODIMERIC FOKI NUCLEASE DOMAIN ELD, UNDER THE CONTROL OF AN APOLIPOPROTEIN E HEPATIC CONTROL REGION AND HUMAN ALPHA-1-ANTITRYPSIN PROMOTER (APOE/HAAT); REC. INN LIST 84