(INNS)
RIVUNATPAGEN MIZIPARVOVEC(INND)
RIVUNATPAGEN MIZIPARVOVEK(INNC)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR ENCODING ATPASE COPPERTRANSPORTING BETA GENE (ATP7B, COPPER TRANSPORTING ATPASE 2), MODIFIED TO ENCODE THE LAST THREE OF THE SIX METAL-BINDING DOMAINS (ATP7B-MBD456), UNDER CONTROL OF A MURINE TRANSTHYRETIN ENHANCER/HUMAN TRANSTHYRETIN PROMOTER, WITH A SIMIAN VIRUS 40 (SV40) INTRON, TERMINATED WITH AN SV40 POLYADENYLATION SIGNAL, AND FLANKED BY ADENO-ASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS (ITRS).(WHO)
RIVUNATPAGENUM MIZIPARVOVECUM(INN)