(INNS)
SEGLEBEGAGEN DASNIPARVOVEC(INND)
SEGLEBEGAGEN DASNIPARVOVEK(INNC)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE HU68 (RAAVHU68) VECTOR ENCODING CODONOPTIMISED HUMAN BETA-GALACTOSIDASE (GLB1), UNDER CONTROL OF THE HUMAN UBIQUITIN C PROMOTER PLUS A CHIMERIC INTRON, CONSISTING OF HUMAN BETA-GLOBIN SPLICE DONOR AND IMMUNOGLOBULIN G SPLICE ACCEPTOR ELEMENTS, TERMINATED WITH THE SIMIAN VIRUS 40 (SV40) LATE POLYADENYLATION SIGNAL, FLANKED BY ADENOASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS (ITRS).(WHO)
SEGLEBEGAGENUM DASNIPARVOVECUM(INN)