AUTOLOGOUS CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS (HSPCS) DERIVED FROM APHERESIS PERIPHERAL BLOOD COLLECTION OF TRANSFUSION DEPENDENT BETA-THALASSEMIA PATIENTS, GENETICALLY MODIFIED AT THE +58 ERYTHROID SPECIFIC ENHANCER REGION OF THE BCL11A GENE BY CRISPR/CAS9 (CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEATS/CRISPR-ASSOCIATED PROTEIN 9) GENE EDITING. ... PROPOSED INN: LIST 131, RECOMMENDED INN: LIST 93(WHO)