(INNS)
ZICLUMERAN(INND)
ZIKLUMERAN(INNC)
MESSENGER RNA (MRNA), 5' CAPPED, ENCODING CODON-OPTIMISED CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEATS (CRISPR) ASSOCIATED PROTEIN 9 (CAS9), FLANKED BY UNTRANSLATED REGIONS (UTR) WITH SIGNIFICANT SEQUENCE HOMOLOGY TO THE XENOPUS BETA GLOBIN GENE, AND TERMINATED WITH A POLYADENYLATION (POLYA) TAIL. A KOZAK SEQUENCE PRECEDES THE OPEN READING FRAME AND THE 5' CAP IS A SYNTHETIC ANTI-REVERSE CAP ANALOGUE (ARCA); CONTAINS N^1- METHYLPSEUDOURIDINE INSTEAD OF URIDINE (ALL-U>M1^PSI)(WHO)
ZICLUMERANUM(INN)