(INNS)
ZOCAGLUSAGEN NUZAPARVOVEC(INND)
ZOKAGLUSAGEN NUZAPARVOVEK(INNC)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 8 (RAAV8) VECTOR ENCODING CODON-OPTIMISED HUMAN ACID ALPHA-GLUCOSIDASE (GAA), ALSO CALLED LYSOSOMAL ALPHA-GLUCOSIDASE OR ACID MALTASE, UNDER CONTROL OF A MOUSE MUSCLE CREATINE KINASE (MCK) ENHANCER/PROMOTER FOLLOWED BY A SIMIAN VIRUS 40 (SV40) INTRON, TERMINATED BY THE SV40 LATE POLYADENYLATION SEQUENCE, AND FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS)(WHO)
ZOCAGLUSAGENUM NUZAPARVOVECUM(INN)